Long-term therapeutic efficacy of allogenic bone marrow transplantation in a patient with mucopolysaccharidosis IVA.

Publication Year: 2014

DOI:
10.1016/j.ymgmr.2013.11.002

PMCID:
PMC4292891

PMID:
25593792

Journal Information

Full Title: Mol Genet Metab Rep

Abbreviation: Mol Genet Metab Rep

Country: Unknown

Publisher: Unknown

Language: N/A

Publication Details

Subject Category: Genetics & Heredity

Available in Europe PMC: Yes

Available in PMC: Yes

PDF Available: No

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Evidence found in paper:

"Conflict of interest All the authors contributed to the Original Article and have no conflict of interest with any other party. Yasutsugu Chinen, Takeshi Higa, Yasuyuki Suzuki, Tadao Orii, Shunji Tomatsu, and Nobuyuki Hyakuna declare that they have no conflict of interests."

Evidence found in paper:

"S.T. was supported by the National Institutes of Health grant 5 P20 RR020173-07. The content of the article has not been influenced by the sponsors. We thank the Morquio A family for kindly providing the consent for the clinical pictures. Editorial assistance to the manuscript was provided by Michelle Stofa at Nemours/Alfred I. duPont Hospital for Children."

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Open Access
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Last Updated: Aug 05, 2025