Deflazacort vs prednisone treatment for Duchenne muscular dystrophy: A meta-analysis of disease progression rates in recent multicenter clinical trials.

"CONFLICT OF INTEREST C.M.M. has served as a consultant for clinical trials for PTC Therapeutics, Inc, and outside the submitted work: BioMarin Pharmaceutical, Sarepta Therapeutics, Eli Lilly and Company, Pfizer, Inc., Santhera Pharmaceuticals, Cardero Therapeutics, Inc, Catabasis Pharmaceuticals, Capricor Therapeutics, Astellas, and FibroGen, Inc; serves on external advisory boards related to Duchenne muscular dystrophy for PTC Therapeutics, Inc., Eli Lilly and Company, Sarepta Therapeutics, Santhera Pharmaceuticals, and Capricor Therapeutics; and reports grants from the US Department of Education/National Institute on Disability and Rehabilitation Research, National Institute on Disability Independent Living and Rehabilitation Research, US National Institutes of Health/National Institute of Arthritis and Musculoskeletal and Skin Diseases, US Department of Defense, and Parent Project Muscular Dystrophy US, during the conduct of the study. P.B.S. has served as an ad‐hoc advisory board member for AveXis, Biogen, Marathon, PTC Therapeutics, Inc, and Sarepta Therapeutics, but he has no financial interests in these companies. He has received research support from Ionis Pharmaceuticals and Biogen for their spinal muscle atrophy (SMA) studies, as well as from Cytokinetics for their SMA clinical trial; Sarepta for their DMD clinical trials; PTC Therapeutics for their DMD/ataluren trial; Pfizer for their DMD/myostatin clinical trial; Bristol‐Myers Squibb/Roche for their DMD/myostatin clinical trial; Sanofi Genzyme for their Pompe clinical trial; and Summit Therapeutics for their DMD clinical trial. B.T.D. has served as an ad‐hoc scientific advisory board member for AveXis, Biogen, Cytokinetics, Marathon Pharmaceuticals, PTC Therapeutics, Bristol‐Myers Squibb, Roche, and Sarepta Therapeutics, but he has no financial interests in these companies. He has received research support from the National Institutes of Health/National Institute of Neurological Disorders and Stroke, the Slaney Family Fund for SMA, the Spinal Muscular Atrophy Foundation, CureSMA, and Working on Walking Fund; grants from Ionis Pharmaceuticals, Inc, for the ENDEAR, CHERISH, and CS1/CS2/CS10/CS12 studies; grants from Biogen for CS11, as well as from Cytokinetics, Sarepta Pharmaceuticals, PTC Therapeutics, FibroGen, and Summit Therapeutics. G.E., M.S., and S.W.P. are employees and stockholders of PTC Therapeutics. G.S., Z.Y., and J.S. are employees of Analysis Group. E.M. was an employee of Analysis Group, at the time this study was conducted. Analysis Group received funding from PTC Therapeutics for this research."

"Funding information Collaborative Trajectory Analysis Project (cTAP); PTC Therapeutics, Inc."