One drug to treat many diseases: unlocking the economic trap of rare diseases.
Journal Information
Full Title: Metab Brain Dis
Abbreviation: Metab Brain Dis
Country: Unknown
Publisher: Unknown
Language: N/A
Publication Details
Related Papers from Same Journal
Transparency Score
Transparency Indicators
Click on green indicators to view evidence textCore Indicators
"Conflict of interest The authors declare no conflicts of interest."
"Funding The work of the authors on rare diseases is supported by the National Science Center (project grant nos. 2017/25/N/NZ2/00812 to KP and 2017/25/B/NZ2/00414 to GW). KP acknowledges the award from the L’Oréal-UNESCO Program “For Women in Science”, and the scholarship from the Foundation for Polish Science within the program “Start”. The funding sources had no involvement in this work at any stage and in the decision to submit the paper for publication. Neither the medical writer nor the editor has been involved in the preparation of this paper."
Additional Indicators
Assessment Info
Tool: rtransparent
OST Version: N/A
Last Updated: Aug 05, 2025