Early experiences of nusinersen for the treatment of spinal muscular atrophy: Results from a large survey of patients and caregivers.

"CONFLICT OF INTEREST Study funded by Genentech Inc., A member of the Roche Group. Er Chen is an employee of GNE. Rupali Naik is a contracting employee of GNE. Josh M Noone, Daniel Buchenberger, Sarah M Whitmire and Rosalina Mills received research funding from GNE for the design and conduct of the research and writing of the paper. Stacy Dixon was contracted with GNE as clinical advisor of this project, no financial compensation was provided. Previously served as a paid member for an advisory board for Genentech. Additionally, have served as a paid member on several advisory boards for Biogen. William Arnold was contracted with GNE as clinical advisor of this project, no financial compensation was provided. Previously served as a consultant to Genentech and F. Hoffmann‐La Roche AG."