Safety and efficacy of nusinersen in spinal muscular atrophy: The EMBRACE study.

"CONFLICT OF INTEREST G.A. has participated in advisory boards for AveXis/Novartis, Biogen, Genentech, and Sarepta; and has participated in consultation and speaker engagements for Biogen. T.O.C. has been an advisor/consultant for AveXis/Novartis, Biogen, Catalyst, Cure SMA, Cytokinetics, Marathon, Novartis, Roche, Sarepta, and the SMA Foundation. W.M.‐F. has participated in advisory boards for AveXis/Novartis, Biogen, PTC, Roche, and Sarepta; has received honoraria from AveXis/Novartis, Biogen, and PTC; has received research funding from BMBF; and has clinical trial research contracts with Biogen, Santhera, and Sarepta. P.B.S. has participated in advisory boards for Biogen and, outside of the submitted work, has participated in advisory boards for AveXis/Novartis, PTC, and Sarepta. R.R. has participated in advisory boards for AveXis/Novartis and Biogen, and has clinical trial research contracts with Biogen. N.N. has received research funding from Biogen for execution of clinical trial projects and National Institutes of Health funding for site principal investigator work on the HEAL‐EEG study. D.C. has participated in advisory board for AveXis/Novartis, Biogen, PTC, and Sarepta; has received research funding from AveXis/Novartis, Biogen, FibroGen, PTC, ReveraGen, and Sarepta; and has participated in medical advisory boards for GBS‐CIDP Foundation, Myasthenia Gravis Foundation, and the Cure SMA Care Center Network. D.R.‐S., G.G., P.S., and W.F. are employees of and hold stock/stock options in Biogen."

"Funding information Biogen (Cambridge, MA); Ionis Pharmaceuticals, Inc (Carlsbad, CA)."