Long-term efficacy and safety of dichlorphenamide for treatment of primary periodic paralysis.

"CONFLICT OF INTEREST Funding for medical writing and editorial assistance was provided by Strongbridge Biopharma, Trevose, PA. V.A.S. has served as a scientific consultant on advisory boards for AveXis, Biogen Idec, Dyne Therapeutics, PTC Therapeutics, Santhera, Sarepta Therapeutics, and for the Italian Spinal Muscular Atrophy Association. N.E.J. has received research support from the Centers for Disease Control and Prevention, Dyne Therapeutics, US Food and Drug Administration, Fulcrum Therapeutics, Muscular Dystrophy Association, Myotonic Dystrophy Foundation, National Institute of Neurological Disorders and Stroke, and Sarepta Therapeutics, and has served as a consultant for AMO Pharma, AskBio, Dyne Therapeutics, Sarepta Therapeutics, Triplet Therapeutics, and Strongbridge Biopharma. E.C. has received personal compensation for serving on advisory boards and/or as a consultant for AveXis, Biogen, Pfizer, PTC Therapeutics, Santhera, Sarepta Therapeutics, and Strongbridge Biopharma, and has received research support from the Centers for Disease Control and Prevention, Cure SMA, US Food and Drug Administration, the Muscular Dystrophy Association, National Institutes of Health, PCORI, Parent Project Muscular Dystrophy, PTC Therapeutics, Santhera, and Sarepta Therapeutics. J.M.S. has received research support from the FSHD Society, Muscular Dystrophy Association, and the National Institutes of Health, and has served as a consultant for Acceleron Pharma, Expansion Therapeutics, Fulcrum Therapeutics, Genea Biocells, and Strongbridge Biopharma. P.B.S. has received grant funding from Acceleron Pharma, Biogen, Fulcrum Therapeutics, the Muscular Dystrophy Association, the National Institutes of Health (NIH), Pfizer, PTC Therapeutics, Roche, Sanofi, and Sarepta Therapeutics, and has served as a consultant for Argenx, Alexion Pharmaceuticals, AveXis, Biogen, Catalyst Pharmaceuticals, Genentech, and Sarepta Therapeutics. F.C. is an employee of Strongbridge Biopharma. R.C.G. has received grant funding from the Muscular Dystrophy Association, the NIH, Parent Project Muscular Dystrophy, PTC Therapeutics, and Sarepta Therapeutics; served as a consultant for PTC Therapeutics, Sarepta Therapeutics, and Strongbridge Biopharma, and served on a data safety monitoring board for Solid Biosciences and Santhera Pharmaceuticals. M.G.H. declares no conflicts of interest."

"Funding information FDA Orphan Drug Program, Grant/Award Number: FD‐R‐000821; NIH National Institute of Neurological Disorders and Stroke, Grant/Award Number: grant R01 NS045686; Strongbridge Biopharma funded post hoc analysis, funded technical editorial assistance"