A novel protein truncating mutation in L2HGDH causes L-2-hydroxyglutaric aciduria in a consanguineous Pakistani family.

Publication Year: 2021

DOI:
10.1007/s11011-021-00832-2

PMCID:
PMC8748340

PMID:
34719772

Journal Information

Full Title: Metab Brain Dis

Abbreviation: Metab Brain Dis

Country: Unknown

Publisher: Unknown

Language: N/A

Publication Details

Subject Category: Metabolism

Available in Europe PMC: Yes

Available in PMC: Yes

PDF Available: No

Transparency Score
3/6
50.0% Transparent
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Evidence found in paper:

"Declarations Ethics approval and consent to participateThe present molecular study was approved by the institutional ethical review board of Gomal University D.I.Khan (IRB# 04/ ERB/GU), and Kohat University of Science and Technology, Kohat, Pakistan. Consent to PublishThe patient’s guardians have given their consent to publish their clinical information and photographs. Conflict of interest/ Competing interestsNone declare by all authors. Conflict of interest/ Competing interests None declare by all authors."

Evidence found in paper:

"Funding The current study was supported through an HEC Pakistan funded “NRPU grant (5564/KPK/NRPU/R&D/HEC/2016)”."

Protocol Registration
Open Access
Paper is freely available to read
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OST Version: N/A

Last Updated: Aug 05, 2025