Timing is everything: Clinical courses of Hunter syndrome associated with age at initiation of therapy in a sibling pair.

Authors:
Grant N; Sohn YB; Ellinwood NM; Okenfuss E; Mendelsohn BA and 4 more

Journal:
Mol Genet Metab Rep

Publication Year: 2022

DOI:
10.1016/j.ymgmr.2022.100845

PMCID:
PMC8856919

PMID:
35242576

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Journal Information

Full Title: Mol Genet Metab Rep

Abbreviation: Mol Genet Metab Rep

Country: Unknown

Publisher: Unknown

Language: N/A

Publication Details

Subject Category: Genetics & Heredity

Available in Europe PMC: Yes

Available in PMC: Yes

PDF Available: No

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"Funding Supported by the Neurodevelopmental Program in Rare Disease, 10.13039/100007249University of Minnesota."

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Last Updated: Aug 05, 2025