Evaluation of diversity indices to estimate clonal dominance in gene therapy studies.

Authors:
Corre G; Galy A.

Journal:
Mol Ther Methods Clin Dev

Publication Year: 2023

DOI:
10.1016/j.omtm.2023.05.003

PMCID:
PMC10220254

PMID:
37251980

View on PubMed View on PMC View Publisher
Journal Information

Full Title: Mol Ther Methods Clin Dev

Abbreviation: Mol Ther Methods Clin Dev

Country: Unknown

Publisher: Unknown

Language: N/A

Publication Details

Subject Category: Medicine, Research & Experimental

Available in Europe PMC: Yes

Available in PMC: Yes

PDF Available: No

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Transparency Score
4/6
66.7% Transparent
Transparency Indicators
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Core Indicators
Data Sharing
Evidence found in paper:

"scripts are available at https://github com/gcorre/genetherapyclonaldiversityindex_study .; scripts are available at https://github com/gcorre/genetherapyclonaldiversityindex_study ."

Evidence found in paper:

"Declaration of interests The authors declare no competing interests."

Evidence found in paper:

"The authors would like to thank Dr. F. Bushman for critical review of the manuscript and acknowledge the contribution of patients, clinicians, and scientists involved in the studies presented. The authors would like to acknowledge the financial support of 10.13039/100007393AFM/Telethon, the 10.13039/100013465French Muscular Dystrophy Association."

Protocol Registration
Open Access
Paper is freely available to read
Additional Indicators
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Novelty Statement
Assessment Info

Tool: rtransparent

OST Version: N/A

Last Updated: Aug 05, 2025