Predictors of 6-year event-free survival in Alagille syndrome patients treated with maralixibat, an ileal bile acid transporter inhibitor.

Authors:
Sokol RJ; Gonzales EM; Kamath BM; Baker A; Vig P and 5 more

Journal:
Hepatology

Publication Year: 2023

DOI:
10.1097/HEP.0000000000000502

PMCID:
PMC10653287

PMID:
37278241

Journal Information

Full Title: Hepatology

Abbreviation: Hepatology

Country: Unknown

Publisher: Unknown

Language: N/A

Publication Details

Subject Category: Gastroenterology

Available in Europe PMC: Yes

Available in PMC: Yes

PDF Available: No

Transparency Score
3/6
50.0% Transparent
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Evidence found in paper:

"CONFLICTS OF INTEREST Ronald J. Sokol advises and consults for Albireo. He advises Mirum. He consults for Alexion. Emmanuel M. Gonzales consults for and advises Albireo and Mirum. He consults for Laboratoires CTRS and Vivet Therapeutics. Binita M. Kamath consults for and received grants from Mirum and Albireo. She consults for Audentes. Alastair Baker received grants from Mirum and Albireo. Pamela Vig owns stock in and is employed by Mirum. Douglas B. Mogul owns stock in and is employed by Mirum. Will Garner owns stock in and is employed by Mirum. Bettina E. Hansen consults for and received grants from Intercept, Calliditas, and Cymabay. She consults for Ipsen, Alberio, Mirum, Enyo, and Eiger. Emmanuel Jacquemin consults for Laboratoire CTRS and Vivet Therapeutics. Richard J. Thompson consults for and owns stock in GenerationBio and Rectify Therapeutics. He consults for Mirum and Albireo."

Evidence found in paper:

"FUNDING INFORMATION This study was supported by Mirum Pharmaceuticals Inc."

Protocol Registration
Open Access
Paper is freely available to read
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Tool: rtransparent

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Last Updated: Aug 05, 2025