Prevention of early-onset cardiomyopathy in <i>Dmd</i> exon 52-54 deletion mice by CRISPR-Cas9-mediated exon skipping.

Publication Year: 2023

DOI:
10.1016/j.omtm.2023.07.004

PMCID:
PMC10403712

PMID:
37545481

Journal Information

Full Title: Mol Ther Methods Clin Dev

Abbreviation: Mol Ther Methods Clin Dev

Country: Unknown

Publisher: Unknown

Language: N/A

Publication Details

Subject Category: Medicine, Research & Experimental

Available in Europe PMC: Yes

Available in PMC: Yes

PDF Available: No

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3/6
50.0% Transparent
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"Declaration of interests The authors declare no competing interests."

Evidence found in paper:

"We acknowledge the members of the Cohn and Delgado laboratories for their input and technical support. We also would like to thank The Center for Phenogenomics for mouse husbandry and A. Flenniken, D. Qu (The Center for Phenogenomics), and the D. Drucker lab (Lunenfeld-Tanenbaum Research Institute) for help with echocardiography. This study was funded by the 10.13039/501100000024Canadian Institutes of Health Research (6210100686) and Jesse’s Journey (6100100206). T.W.Y.W. was funded by a Restracomp Award (SickKids–University of Toronto Ontario Student Opportunity Trust Fund) and an Ontario Graduate Scholarship. P.D.-O. is supported by the 10.13039/501100000024Canadian Institutes of Health Research (CIHR) (162208, 149046, and 468633)."

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Last Updated: Aug 05, 2025