In-depth comparison of Anc80L65 and AAV9 retinal targeting and characterization of cross-reactivity to multiple AAV serotypes in humans.

Journal Information

Full Title: Mol Ther Methods Clin Dev

Abbreviation: Mol Ther Methods Clin Dev

Country: Unknown

Publisher: Unknown

Language: N/A

Publication Details

Subject Category: Medicine, Research & Experimental

Available in Europe PMC: Yes

Available in PMC: Yes

PDF Available: No

Transparency Score
3/6
50.0% Transparent
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Evidence found in paper:

"Declaration of interests K.M. is receiving royalties from Gene Therapy programs licensed to Amicus Therapeutics and Kiadis. K.M. is a scientific advisor with compensation and stock options and has received research funding from Alcyone Therapeutics."

Evidence found in paper:

"We would like to especially thank Dr. Luk Vandenberghe for publically providing the An80 capsid for vector generation. Thank you to SAB Tech Inc. for producing the vectors described in this study and their commitment to quality. Thank you to the Animal Resource Core at NCH for maintaining the high quality of care provided to our animals. This study was funded by internal funds of the Abigail Wexner Research Institute, Nationwide Children's Hospital."

Protocol Registration
Open Access
Paper is freely available to read
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Assessment Info

Tool: rtransparent

OST Version: N/A

Last Updated: Aug 05, 2025