Establishing Patient-Centered Outcomes for MCT8 Deficiency: Stakeholder Engagement and Systematic Literature Review.

Publication Year: 2023

DOI:
10.2147/NDT.S379703

PMCID:
PMC10595182

PMID:
37881807

Journal Information

Full Title: Neuropsychiatr Dis Treat

Abbreviation: Neuropsychiatr Dis Treat

Country: Unknown

Publisher: Unknown

Language: N/A

Publication Details

Subject Category: Clinical Neurology

Available in Europe PMC: Yes

Available in PMC: Yes

PDF Available: No

Transparency Score
3/6
50.0% Transparent
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Core Indicators
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Evidence found in paper:

"Disclosure Professor Catherine Sarret reports personal fees from EGETIS, during the conduct of the study; personal fees from NOVARTIS, ARGENX, ORCHARD, and LUPIN, outside the submitted work. The authors report no other conflicts of interest in this work."

Evidence found in paper:

"NMW was supported by the DFG Research Unit 2841 “Beyond the Exome”. HK und MS were supported by the DFG P06 of TRR 296 “Local control of TH action” (LocoTact)."

Protocol Registration
Open Access
Paper is freely available to read
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Assessment Info

Tool: rtransparent

OST Version: N/A

Last Updated: Aug 05, 2025