Clinical features of acute attacks, chronic symptoms, and long-term complications among patients with acute hepatic porphyria in Japan: a real-world claims database study.

Journal Information

Full Title: Orphanet J Rare Dis

Abbreviation: Orphanet J Rare Dis

Country: Unknown

Publisher: Unknown

Language: N/A

Publication Details

Subject Category: Medicine

Available in Europe PMC: Yes

Available in PMC: Yes

PDF Available: No

Transparency Score
3/6
50.0% Transparent
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Evidence found in paper:

"Declarations Ethics approval and consent to participateNot applicable; database study using deidentified and anonymous data. Consent for publicationNot applicable; database study using deidentified and anonymous data. Competing interestsYH reported receiving consultant fees from Alnylam Japan KK. YY reported being employed by Alnylam Japan KK and owning stock or stock options in Alnylam Pharmaceuticals. TA declares that he has no competing interests. Competing interests YH reported receiving consultant fees from Alnylam Japan KK. YY reported being employed by Alnylam Japan KK and owning stock or stock options in Alnylam Pharmaceuticals. TA declares that he has no competing interests."

Evidence found in paper:

"Funding This study was funded by Alnylam Japan KK. Data from the Medical Data Vision database were used, and data analysis was performed by Intage Healthcare Inc., under the direction of the study authors, and funded by Alnylam Japan KK. Medical writing support and editorial support were provided by Peloton Advantage, L.L.C., an OPEN Health company, and funded by Alnylam Japan KK."

Protocol Registration
Open Access
Paper is freely available to read
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Assessment Info

Tool: rtransparent

OST Version: N/A

Last Updated: Aug 05, 2025