Real life data: follow-up assessment on Spanish Gaucher disease patients treated with eliglustat. TRAZELGA project.

Journal Information

Full Title: Orphanet J Rare Dis

Abbreviation: Orphanet J Rare Dis

Country: Unknown

Publisher: Unknown

Language: N/A

Publication Details

Subject Category: Medicine

Available in Europe PMC: Yes

Available in PMC: Yes

PDF Available: No

Transparency Score
3/6
50.0% Transparent
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Evidence found in paper:

"Declarations Ethics approvalThe study was approved by the Research Ethics Committee of the Autonomous Community of Aragon (CEICA) and classify by the AEMPS as EPA-SP (ID: GEE-ELI 2017–01). Consent to participateInformed consent was obtained from all subjects involved in the study. All authors consent for publication and accepted the last version of the manuscript. Competing interestsLaura López de Frutos Ph.D. is an employee of Azafaros B.V. outside the submitted work without stock options. Competing interests Laura López de Frutos Ph.D. is an employee of Azafaros B.V. outside the submitted work without stock options."

Evidence found in paper:

"Funding TRAZELGA (GZ-2017-11713) received a grant from Sanofi for its realization. The work has been partially granted by a FEETEG Research Grant (ID#1703)."

Protocol Registration
Open Access
Paper is freely available to read
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Assessment Info

Tool: rtransparent

OST Version: N/A

Last Updated: Aug 05, 2025