Iron oxide-coupled CRISPR-nCas9-based genome editing assessment in mucopolysaccharidosis IVA mice.

Publication Year: 2023

DOI:
10.1016/j.omtm.2023.101153

PMCID:
PMC10724691

PMID:
38107675

Journal Information

Full Title: Mol Ther Methods Clin Dev

Abbreviation: Mol Ther Methods Clin Dev

Country: Unknown

Publisher: Unknown

Language: N/A

Publication Details

Subject Category: Medicine, Research & Experimental

Available in Europe PMC: Yes

Available in PMC: Yes

PDF Available: No

Transparency Score
3/6
50.0% Transparent
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Evidence found in paper:

"Declaration of interests The authors declare no conflict of interest."

Evidence found in paper:

"A.F.L. received a PhD scholarship from Pontificia Universidad Javeriana. C.J.A.D was supported by 10.13039/501100009543Pontificia Universidad Javeriana (Investigar PUJ 20386, 20567, and 20646), Ministry of Science, Technology, and Innovation from Colombia (Contract 120380763212, ID 8352, and CT-499-2021, ID 9630), and the 10.13039/100013927National MPS Society (ID 9507). This work was also supported by grants from the Austrian MPS society, A Cure for Robert, Inc., The Carol Ann Foundation, Angelo R. Cali & Mary V. 10.13039/100002769Couch Family Foundation, Inc., The Vain and 10.13039/100006810Hyde Family Foundation, Inc., 10.13039/100018298The Bennett Foundation, Jacob Randall Foundation, and Nemours Funds. S.T. was supported by an Institutional Development Award from the Eunice Kennedy Shriver National Institute of Child Health & Human Development of the National Institutes of Health (NICHD) (1R01HD10254501A1)."

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Open Access
Paper is freely available to read
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Tool: rtransparent

OST Version: N/A

Last Updated: Aug 05, 2025