A position statement on the post gene-therapy rehabilitation of aromatic I-amino acid decarboxylase deficiency patients.
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Full Title: Orphanet J Rare Dis
Abbreviation: Orphanet J Rare Dis
Country: Unknown
Publisher: Unknown
Language: N/A
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"Declarations Ethics approval and consent to participateNot applicable. Consent for publicationNot applicable. Competing interestsREP and JW declare that they have no competing interests. AK and JT are employees of PTC Therapeutics, Inc. H-ML, SM-A, GH, and DM have served as advisory board members for PTC Therapeutics, Inc. W-LH has served as an advisory board member, consulted for, and received research grants from PTC Therapeutics, Inc. Competing interests REP and JW declare that they have no competing interests. AK and JT are employees of PTC Therapeutics, Inc. H-ML, SM-A, GH, and DM have served as advisory board members for PTC Therapeutics, Inc. W-LH has served as an advisory board member, consulted for, and received research grants from PTC Therapeutics, Inc."
"Funding Funding for this article was provided by PTC Therapeutics, Inc."
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Last Updated: Aug 05, 2025