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Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping…
Clemens PR; Rao VK; Connolly AM; Harper AD; Mah JK; Smith EC; McDonald CM; Zaidman CM; Morgenroth LP; Osaki H; Satou Y; Yamashita T; Hoffman EP; CINRG DNHS Investigators.
JAMA Neurol
(Unknown)
Published: 2020
Use of Multimodal Imaging and Clinical Biomarkers in Presymptomatic Carriers of C9orf72 Repeat Expansion.
De Vocht J; Blommaert J; Devrome M; Radwan A; Van Weehaeghe D; De Schaepdryver M; Ceccarini J; Rezaei A; Schramm G; van Aalst J; Chiò A; Pagani M; Stam D; Van Esch H; Lamaire N; Verhaegen M; Mertens N; Poesen K; van den Berg LH; van Es MA; Vandenberghe R; Vandenbulcke M; Van den Stock J; Koole M; Dupont P; Van Laere K; Van Damme P.
JAMA Neurol
(Unknown)
Published: 2020
Diagnostic Performance of RO948 F 18 Tau Positron Emission Tomography in the Differentiation of Alzheimer Disease From …
Leuzy A; Smith R; Ossenkoppele R; Santillo A; Borroni E; Klein G; Ohlsson T; Jögi J; Palmqvist S; Mattsson-Carlgren N; Strandberg O; Stomrud E; Hansson O.
JAMA Neurol
(Unknown)
Published: 2020
Effect of an Enhanced Paramedic Acute Stroke Treatment Assessment on Thrombolysis Delivery During Emergency Stroke Care…
Price CI; Shaw L; Islam S; Javanbakht M; Watkins A; McMeekin P; Snooks H; Flynn D; Francis R; Lakey R; Sutcliffe L; McClelland G; Lally J; Exley C; Rodgers H; Russell I; Vale L; Ford GA.
JAMA Neurol
(Unknown)
Published: 2020
Dose-Ranging Effect of Adjunctive Oral Cannabidiol vs Placebo on Convulsive Seizure Frequency in Dravet Syndrome: A Ran…
Miller I; Scheffer IE; Gunning B; Sanchez-Carpintero R; Gil-Nagel A; Perry MS; Saneto RP; Checketts D; Dunayevich E; Knappertz V; GWPCARE2 Study Group.
JAMA Neurol
(Unknown)
Published: 2020
Ambroxol for the Treatment of Patients With Parkinson Disease With and Without Glucocerebrosidase Gene Mutations: A Non…
Mullin S; Smith L; Lee K; D'Souza G; Woodgate P; Elflein J; Hällqvist J; Toffoli M; Streeter A; Hosking J; Heywood WE; Khengar R; Campbell P; Hehir J; Cable S; Mills K; Zetterberg H; Limousin P; Libri V; Foltynie T; Schapira AHV.
JAMA Neurol
(Unknown)
Published: 2020
Nilotinib Effects on Safety, Tolerability, and Potential Biomarkers in Parkinson Disease: A Phase 2 Randomized Clinical…
Pagan FL; Hebron ML; Wilmarth B; Torres-Yaghi Y; Lawler A; Mundel EE; Yusuf N; Starr NJ; Anjum M; Arellano J; Howard HH; Shi W; Mulki S; Kurd-Misto T; Matar S; Liu X; Ahn J; Moussa C.
JAMA Neurol
(Unknown)
Published: 2020
Selective Vulnerability of the Nucleus Basalis of Meynert Among Neuropathologic Subtypes of Alzheimer Disease.
Hanna Al-Shaikh FS; Duara R; Crook JE; Lesser ER; Schaeverbeke J; Hinkle KM; Ross OA; Ertekin-Taner N; Pedraza O; Dickson DW; Graff-Radford NR; Murray ME.
JAMA Neurol
(Unknown)
Published: 2020
Association of Concussion Symptoms With Testosterone Levels and Erectile Dysfunction in Former Professional US-Style Fo…
Grashow R; Weisskopf MG; Miller KK; Nathan DM; Zafonte R; Speizer FE; Courtney TK; Baggish A; Taylor HA; Pascual-Leone A; Nadler LM; Roberts AL.
JAMA Neurol
(Unknown)
Published: 2019