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Marmosets as a preclinical model for testing "off-label" use of doxycycline to turn on Flt3L expression from high-capac…
VanderVeen N; Paran C; Appelhans A; Krasinkiewicz J; Lemons R; Appelman H; Doherty R; Palmer D; Ng P; Lowenstein PR; Castro MG.
Mol Ther Methods Clin Dev
(Unknown)
Published: 2014
Targeted CNS Delivery Using Human MiniPromoters and Demonstrated Compatibility with Adeno-Associated Viral Vectors.
de Leeuw CN; Dyka FM; Boye SL; Laprise S; Zhou M; Chou AY; Borretta L; McInerny SC; Banks KG; Portales-Casamar E; Swanson MI; D'Souza CA; Boye SE; Jones SJ; Holt RA; Goldowitz D; Hauswirth WW; Wasserman WW; Simpson EM.
Mol Ther Methods Clin Dev
(Unknown)
Published: 2014